Panel Discussion: Refining Sensitive Primary Outcome Measures & Navigating Innovative Trial Design in ALS

Time: 2:00 pm
day: Day One


  • Pursuing sensitive markers of disease activity and delineating accurate primary outcome measures beyond ALSFRS-R
  • Driving early diagnosis, patient diversity, and decentralized trial design to establish effective patient recruitment
  • Can we capture statistically meaningful changes in an acute timeframe? Balancing length of trial to demonstrate safety and clinical benefit