Pioneering Gene Editing for ALS: Advancing ABO-202 and a Pipeline of CNS-Directed Therapeutics

Time: 1:30 pm
day: Conference Day Two Track B PM

Details:

  • Introducing Arbor’s gene editing platform and unique commitment to CNS and ALS
  • Deep dive into ABO-202: AAV-delivered gene editing approach targeting STMN2 to restore protective neuronal function
  • Preclinical data supporting progression of ABO-202 toward IND-enabling studies
  • Future directions for Arbor’s gene editing programs in ALS

Speakers: