Reinventing SOD1 Targeting with CRISPR-Based Gene Editing Technology to Diminish Mutant SOD1 & Restore Motor Neuronal Function
Time: 1:40 pm
day: Day Two Track A PM
Details:
- Demonstrating disruption to the human SOD1 transgene using in vivo gene editing technology
- Revealing functional restoration of motor neurones following intracerebroventricular injection
- Utilizing this CRISPR editing preclinical approach for target evaluation
