Angela Genge

Company: McGill University

Job title: ALS Centre of Excellence

Seminars:

Showcasing Clinical Success of a Novel STMN2-Targeting ASO to Restore Functional Expression & Promote Motor Neuronal Repair 1:40 pm

Outlining latest advancements in the QRL-201 program Achieving successful restoration of STATHMIN-2 expression in ALS patients Highlighting upcoming steps in the advancement of QRL-201 towards later phase studiesRead more

day: Day Two Track B PM

Reinventing the Surrogate Landscape: Innovating Regulatory Acceptable Endpoints Most Meaningful to People Living with ALS 2:05 pm

The recent accelerated approval brings new waves of promise for transformative ALS drugs to be approved based on surrogate markers that correlate with ALSFRS-R. With increasing demand to define more acceptable endpoints for ALS, collaborate with industry sponsors and regulatory experts to: Evaluate the potential of novel surrogate biomarkers that extend beyond ALSFRS-R to monitor…Read more

day: Pre-Conference Day